Research Program | Overview
We continue to be active in research and routinely present our research annually at National and International meetings. In addition, we publish our research regularly in multiple peer reviewed journals.
CURRENTLY OPEN:
Recorded Home Oximetry to Optimize Weaning in Premature Infants
- Sponsor: Boston Children’s Hospital
- Short title: RHO
- Site Investigator: Dr. Sankaran Krishnan
Characterizing CFTR Modulated Changes in Sweat Chloride and their Association with Clinical Outcomes
- Sponsor: Cystic Fibrosis Foundation Therapeutics
- Short title: CHEC
- Clinical Trial Info
- Site Investigator: Dr. Allen Dozor
Cystic Fibrosis Patient Registry
- Sponsor: Cystic Fibrosis Foundation
- Short title: Port CF
- Clinical Trial Info
- Site Investigator: Dr. John Welter
A Phase 1/2a Randomized, Double-Blind, Two-Part, Dose-Ascending, Multicenter Study of the Safety and Pharmacokinetics of AR-501 (gallium citrate) Administered via Inhalation, in Healthy Adult and P. Aeruginosa Infected Cystic Fibrosis Subjects
- Sponsor: Aridis Pharmaceuticals, Inc.
- Short title: AR-501
- Clinical Trial Info
- Site Investigator: Dr. Alison Lennox
A Phase 1B/2A, Multi-Center, Double-Blind, Randmoized, Placebo-Controlled, Single and Multiple Ascending Dose Study to Evaluate the Safety and Tolerability of AP-PA02 Multi-Phage Therapeutic Candidate for Inhalation in Subjects with Cystic Fibrosis and Chronic Pulmonary Pseudomonas Aeruginosa (PA) Infection
- Sponsor: Armata Pharmaceuticals, Inc.
- Short title: SWARM-Pa
- Clinical Trial Info
- Site Investigator: Dr. Alison Lennox
Relationship Between CFTR Function, Ventilation Heterogeneity, and Airway Obstruction in Young Adults
- Sponsor: American Lung Association
- Short title: SCAO
- Site Investigator: Dr. Alison Lennox
A Phase 1, Open-Label, Randomized, Crossover Study to Assess the Safety and Pharmacokinetics Following Single Doses of Oral and Intravenous Xenleta (Lefamulin) in Adult Patients with Cystic Fibrosis
- Sponsor: Nabriva Therapeutics
- Short title: Nabriva
- Clinical Trial Info
- Site Investigator: Dr. John Welter
A Phase 3, Randomized, Double-Blind, Controlled Study Evaluating the Efficacy and Safety of VX-121 Combination Therapy in Subjects with Cystic Fibrosis Who Are Heterozygous for F508del and a Minimal Function Mutation (VX20-121-102)
- Sponsor: Vertex Pharmaceuticals, Inc.
- Short title: Vx-121-102
- Clinical Trial Info
- Site Investigator: Dr. John Welter
Assessment of Intestinal Microbiome in Patients with Cystic Fibrosis with Distal Intestinal Obstruction Syndome
- Sponsor: None
- Short title: ADIOS-CF
- Site Investigator: Dr. Shilpa Sood
The CHRONICLE Study: A Longitudinal Prospective Observational Study of the Characteristics, Treatment Patterns and Health Outcomes of Individuals with Severe Asthma in the United States
- Sponsor: AstraZeneca
- Short title: Chronicle
- Clinical Trial Info
- Site Investigator: Dr. Sankaran Krishnan
ADVOCACY PROJECTS:
- Quality Improvement Work Assessing for the Use of AAR (Assess, Advise, Refer) with Regards to Smoking Cessation Counseling for Children with Environmental Tobacco Smoke Exposure
- Quality Improvement Work on Influenza Vaccine Hesitancy
- The Hudson Valley Carbon Monoxide Detector Advocacy Project