Research

Research at Boston Children's Hospital

The research enterprise at Boston Children’s Hospital, comprising more than 3,000 researchers, is the world’s largest at a pediatric center. Our work is fueled by a deep understanding of disease coupled with world-class discovery platforms, including genetics and genomics, gene editing, bioinformatics, proteomics, bioengineering, image analysis, multiple animal models, biobanks and disease-specific stem cell lines. We have special expertise in rare disease discovery and see large, highly diverse patient populations.

michael rogers and danielle peterse

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More than 3,000 researchers & scientific staff

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1 million square feet of research space — and growing

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$388 million in total research funding FY2018 — #1 NIH funding for pediatric research

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A new frontier: Inside a custom drug

Dr. Yu and his team of scientists pulled off something unprecedented, something seemingly impossible. In the space of 10 months, they pinpointed Mila’s rare mutation, designed a drug to bypass it, engaged industry partners and FDA regulators, and launched a treatment trial — just for Mila.

Early encouraging results are reported in The New England Journal of Medicine. They could open a new path, showing it’s possible to create personalized genetic therapies for children with rare conditions — and to do so quickly.

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Dr. Yu batten disease

Boston Children's Hospital Innovation

BCH Innovation News @BCH_Innovation 11/13/2019 10:00:01 PM
Diet trials are currently underfunded and lack rigor, say @davidludwigmd and @heymsfield in @JAMANetworkOpen and a… https://t.co/3t5bKTG47Z
BCH Innovation News @BCH_Innovation 11/13/2019 9:38:19 PM
RT @MicrobesInfo: Treating #tuberculosis by boosting #immune defences ... | #bacteria | #infection | #disease | #immunity | #TB | #Mtb | #…
BCH Innovation News @BCH_Innovation 11/13/2019 9:38:03 PM
RT @SIMPeds_BCH: More dates added! Feb 24 - 26, 2020 @BostonChildrens New FOUNDATIONS OF SIMULATION INSTRUCTION COURSE, creating essential…
BCH Innovation News @BCH_Innovation 11/13/2019 3:00:01 PM
.@medpagetoday reports the risk of a liver complication for pregnant women with Cirrhosis is lower than originally… https://t.co/fmo9NeqPz7
BCH Innovation News @BCH_Innovation 11/13/2019 2:00:01 PM
FDA-approved drug could boost host immune defenses against #tuberculosis, as well as #Ebola: https://t.co/OinXsMttiW #drugrepurposing
BCH Innovation News @BCH_Innovation 11/12/2019 8:19:18 PM
RT @tomsandora: Check out our study published today in @naturemedicine in which we provide genomic evidence that bacteria from probiotic ca…
Building on our extraordinary leadership in pediatric science at Boston Children’s, we translate our findings — and those of others — to fundamentally change how disease is treated and cured.

David A. Williams, MD
Senior Vice President and Chief Scientific Officer